Generic Ivacaftor is One Step Closer in the US
If you’ve followed my blog for the last year or so, you’ve seen that I’ve been repeatedly...
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Category: Today in Medicine
If Vertex Has Such a Commanding Hold on the CFTR Modulator Market, Why Are Other Drug Makers Joining the Race?
With news of the emerging biotech company, Sionna, coming out of stealth yesterday, there is, once...
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The Race for Cystic Fibrosis Gene Therapies Is On!
Gene therapies are all the rage these days in the world of emerging biotech. It’s not hard to...
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Mark Cuban’s Cost Plus Drug Company Will Provide Much Needed Relief for Drug Costs
If Mark Cuban’s Cost Plus Drug Company (yes, that’s literally the name) can be sustained, it might...
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It is a Gift to Hear Mallory Smith’s Voice in ‘Salt in My Soul’ Documentary
Salt in My Soul, the documentary version, is something special. If you’ve followed the blog for a...
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CFF’s Rapid Fire Deals Prove There is Still a Market for New CF Drugs
The Cystic Fibrosis Foundation has started off the new year with a handful of new investments that...
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Cystic Fibrosis is Changing, and It’s Remarkable
Last week we celebrated news out of the North American Cystic Fibrosis Conference that median age...
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Understanding Median Predicted Survival, Life Expectancy and the Rapid Progress in Cystic Fibrosis
My timelines are on fire with the wonderful news out of the North American Cystic Fibrosis...
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I Have Been in Clinical Trials and Taken Experimental Medications, the COVID-19 Vaccines are Well Beyond that Point
Anytime I hear (or see) someone talking about the Pfizer or Moderna vaccines as if they are...
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Telehealth was an Experiment in CF Care During COVID, Let’s Make it Standard
Times are changing in cystic fibrosis. Anecdotally you hear about patients rapidly withdrawing...
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How Much Money is Spent on Cystic Fibrosis Research and Development?
The answer: A LOT. I decided to do some very rough back-of-the-napkin math to understand spending...
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Moderna’s COVID-19 Vaccine FDA Briefing Mentions Cystic Fibrosis
Since the beginning of the COVID-19 vaccine development process, Moderna has sought to be...
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